As our understanding of achondroplasia progresses and new therapeutic options are developed, it is important to evaluate whether the tools we use in practice are still suitable to accurately assess outcomes.
During our Spring workshop Assessing Outcomes in a New Era of Achondroplasia Treatment Dr Melita Irving lead the discussion with doctors Geneviève Baujat, Sérgio de Sousa and Antonio Leiva-Gea on whether current achondroplasia outcome measures are fit for purpose in the era of therapeutic management, therapeutic management in the real world, as well as the new treatment options in development.